欧美成一级-欧美成在人线a免费-欧美传媒影-欧美大逼逼-欧美大成色www永久网站婷-欧美大胆a级视频

Gene Therapy
The Gene Editing Technology Innovation Platform
Hematopoietic Stem Cell Platform

Hematopoietic Stem Cell Platform

The Hematopoietic Stem Cell Platform (ModiHSC?) uses CRISPR-related gene editing tools, lentiviral vectors and other technologies to genetically modify the hematopoietic stem cells of patients. The modified hematopoietic stem cells are reinjected into patients, and the new blood system is reconstructed through HSC self-renewal and differentiation, so as to cure the disease.?Hematopoietic stem cell gene therapy has the advantages of good targeting, high safety, wide range of application, and significant therapeutic effects, which can achieve a life-long cure with one treatment.?The related research results have been published in top international academic journals such as Nature Medicine, Nature Biotechnology, Cell Research.?Using this platform, our company has developed a cell therapy product for the treatment of β thalassemia. It has successfully cured patients with severe β thalassemia, which is the first successful case in the world to treat β0/β0 severe thalassemia using CRISPR gene editing technology.

Gene therapy fort thalassemia

Thalassemia is a typical monogenic genetic disease caused by mutation or deletion of the pearl protein gene, which mainly includes α- and β- thalassemia. The rate of carrying the gene of thalassemia accounts for about 1.5% of the world population (80-90 million), and about 68,000 children with thalassemia are born every year, which is one of the genetic diseases with the greatest impact and incidence in China. Currently there is no complete cure for hemoglobinopathies, and although some patients use bone marrow transplantation, it is expensive and extremely difficult to match. In recent years, the advent of gene therapy has brought hope to patients, with the greatest advantages of not requiring a donor, not requiring an allogeneic transplant, and the possibility of a single treatment leading to a permanent "cure", promising to replace the current imperfect treatment options. Gene Therapy is the introduction of exogenous normal genes into target cells to correct or compensate for diseases caused by defective and abnormal genes for therapeutic purposes. With its unique potential to cure genetic diseases once administered for life, gene therapy makes the impossible possible. It has shown great therapeutic potential in a variety of diseases such as cancer, genetic disorders such as thalassemia, sickle cell anemia, hemophilia and congenital melanosis.
Back to top
主站蜘蛛池模板: 男男女女爽爽爽免费视频 | 亚洲欧洲精品一区二区三区 | 国内精品91最新在线观看 | 无码日韩精品一区二区免费暖暖 | 国产免费一区二区三区香蕉精 | 日韩精品亚洲成本人专区电影 | 欧美午夜一区二区三区 | 国产在线观看精品香蕉v区 国产在线观看精品一区二区三区 | 国产九九精品 | 91精品国产综合久久久久久久 | 欧美午夜精品久久久久久浪潮 | 足交在线视频亚洲第一 | 欧美毛片aaaaa片久久久久 | 精品国产第一页 | 91日本在线精品高清观看 | 强伦人妻一区二区三 | 日韩免费 | 亚洲一区二区国产精品 | 日日撸影院在线 | 欧美操美女 | 久久国产精品动态图 | 91精品国产自产在线观看永久 | 抖音奶片故意走漏15秒 | 久久久国产99久久国 | 免费人成视频在线观看播放网站 | 国产成人h视频在线观看 | 日本国产高清网色 | 尤蜜精品视 | 国产亚洲av另类一区二区三区 | 国产在线精品一区二区高清 | 国产精品后入内射日本在线观看 | 欧美巨波霸乳影院67194 | 91在线视频免费观看 | 91自产拍在线观看精品 | 无人区一码 | 18禁裸乳无遮挡啪啪无码免费 | 好硬好紧好湿进去了好爽 | 久久98精品久久久久久婷婷 | 极品人妻乳哺乳 | 波多野结衣久久久日本 | 亚洲中文字幕在线无码中出 |